Leveraging Functional Genomics for Discovery of Novel Parkinson’s Disease Targets: From Genetics to Mechanism

  • Integrating human genetics with iPSC-based disease models to recapitulate causal biology and developing isogenic systems that faithfully model PD-relevant risk variants, to accelerate discovery of differentiated, genetically validated targets with higher translational value
  • Using functional genomics and human iPSC-models to uncover new target opportunities for Parkinson’s disease
  • Developing predictive models in iPSC-derived neurons, to provide tractable, disease-relevant efficacy readouts